What is a clinical trial?
Clinical trials are studies conducted to assess medical interventions and treatments by exploring the pathology of diseases, and efficacy of new medications. The aim of trials is to develop better strategies for healthcare and disease management.
Observational research, often referred to as natural history studies, is another type of clinical study. These studies enable clinicians to gather valuable data that helps design effective clinical trials and increase their likelihood of success.
Important information about clinical trials:
If you're interested in a study, let your clinical team know so they can inform the trial site, or contact the trial site directly and they can reach out to your local team.
The registry aims to simplify patient recruitment for trials, but registration doesn't guarantee participation.
Even if trial coordinators think you're eligible based on your registry data, you may later not meet the inclusion criteria.
Many trials are location-specific, so please visit clinicaltrials.gov for up-to-date info on approved trials and sites.
Even if you do not wish to participate in a clinical trial, your information can still make a valuable contribution by helping researchers learn more about FKRP related conditions.
Please find more information below about how clinical trials work. If you have specific questions about what happens if you are eligible for a clinical trial, or about deciding whether to participate, please visit our FAQs section.